Amyotrophic Lateral Sclerosis (ALS)
ALS is a progressive neurodegenerative disease. Median survival is 3 to 5 years and there is no effective treatment or a cure.
Islet Transplant in Type 1 Diabetes (T1D)
Type 1 Diabetes (T1D) is an autoimmune disease with progressive loss of insulin-producing Beta cells in the pancreas and uncontrolled hypoglycemia. There is no effective treatment or cure.
Our team is working with key opinion leaders in Focal Segmental Glomerulosclerosis (FSGS), Sjogren's Syndrome (SS), and neutralizing antibodies to enzyme replacement and gene therapies as potential therapeutic areas